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Muscular Dystrophy

Patient Deaths Reported With Controversial Muscular Dystrophy Drug

Three patient deaths and 8 other serious adverse events have been reported with a controversial drug to treat Duchenne muscular dystrophy, a rare, muscle-wasting disease that predominantly affects young boys. The drug, Exondys 51 (eteplirsen), was approved by the FDA in September 2016. The approval was significant in that the…

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