Medical Conditions

Browse by Category

Muscular Dystrophy

Patient Deaths Reported With Controversial Muscular Dystrophy Drug

Three patient deaths and 8 other serious adverse events have been reported with a controversial drug to treat Duchenne muscular dystrophy, a rare, muscle-wasting disease that predominantly affects young boys. The drug, Exondys 51 (eteplirsen), was approved by the FDA in September 2016. The approval was significant in that the…

  • [class^="wpforms-"]